At PTC, we are committed to a single purpose: Extending life’s moments for patients with rare diseases and their loved ones.
Our mission is to provide access to best-in-class treatments for rare disease patients who have little to no treatment options. Whether our therapies grant hours, days, months or years, every small moment is an enormous win – so our greatest accomplishments are “measured by moments.”
This mission underpins our focus on the discovery, development and global commercialization of clinically differentiated medicines that provide benefits to patients with rare disorders.
As a science-driven, global biopharmaceutical company, we combine our strong clinical and scientific expertise with dedication to using groundbreaking science and new technologies to find innovative ways to treat these diseases, which can give patients and their families more moments.